Natural History Study
CLN5 and CLN7*
A natural history study is an essential component of developing and expediting treatments, where the natural history is not well documented. Participating in a natural history study enables a rigorous scientific evaluation of disease characteristics and disease progression, which provides essential information to design a clinical trial that allows for the evaluation of whether a treatment is safe and effective.
A Natural History Study of Late Infantile Variant CLN5 And CLN7 Disease
*Enrollment for CLN7 patients is full