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OUR PIPELINE
We are building a gene therapy pipeline to help address the high unmet need for rare neurological diseases.
Focusing on the Future of Life-Changing
Genetic Medicines
Gene therapy holds incredible promise to revolutionize medical treatment. At Neurogene we believe that innovation, robust scientific execution, and a strong sense of purpose are required to turn this promise into reality. Our focus is to develop life-changing genetic medicines for people and their families impacted by devastating neurological diseases.
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ABOUT US
At Neurogene, we are driven by a strong sense of purpose to advance genetic medicines.
LATEST NEWS
Neurogene Announces New Development Program in Rett Syndrome Utilizing Novel EXACT Technology Platform
Promising preclinical data for NGN-401 presented at 25th Annual Meeting of the American Society of Gene and Cell Therapy (ASGCT)…
Learn MoreState of the Art Manufacturing
Neurogene owns and operates a state-of-the-art gene therapy manufacturing facility in Houston, Texas with fully integrated process and analytical development, and CGMP capabilities. We have developed two scalable AAV manufacturing processes (mammalian and insect cell-based production) to support preclinical studies and clinical trials.